Neuren Phase 2 trial shows significant improvements in Pitt Hopkins syndrome
- Written by PR Newswire
Highlights:
- Statistically significant improvement from baseline assessed by both clinicians and caregivers in all four efficacy measures specifically designed for Pitt Hopkins syndrome (Wilcoxon signed rank test p<0.05)
- Clinician and caregiver global efficacy measures showed a level of improvement considered clinically meaningful:
- Clinical...







